{"id":8400,"date":"2025-08-04T18:55:44","date_gmt":"2025-08-04T16:55:44","guid":{"rendered":"https:\/\/rvh-synergie.org\/actualites\/la-therapie-cellulaire-empeche-les-dommages-de-la-dystrophie-musculaire-de-duchenne-dans-le-modele-de-souris\/"},"modified":"2025-08-04T18:55:49","modified_gmt":"2025-08-04T16:55:49","slug":"la-therapie-cellulaire-empeche-les-dommages-de-la-dystrophie-musculaire-de-duchenne-dans-le-modele-de-souris","status":"publish","type":"post","link":"https:\/\/rvh-synergie.org\/actualites\/la-therapie-cellulaire-empeche-les-dommages-de-la-dystrophie-musculaire-de-duchenne-dans-le-modele-de-souris\/","title":{"rendered":"La th\u00e9rapie cellulaire emp\u00eache les dommages de la dystrophie musculaire de Duchenne dans le mod\u00e8le de souris"},"content":{"rendered":"<div>\n<div class=\"article-gallery lightGallery\">\n<div data-thumb=\"https:\/\/scx1.b-cdn.net\/csz\/news\/tmb\/2025\/preclinical-study-show.jpg\" data-src=\"https:\/\/scx2.b-cdn.net\/gfx\/news\/hires\/2025\/preclinical-study-show.jpg\" data-sub-html=\"Protection against functional decline in mdx mice by repeated CDC therapy. Credit: &lt;i&gt;Stem Cell Reports&lt;\/i&gt; (2025). DOI: 10.1016\/j.stemcr.2025.102468\">\n<figure class=\"article-img\">\n<\/figure><\/div>\n<\/div>\n<p>Une th\u00e9rapie cellulaire pr\u00e9serve la structure musculaire et la fonction chez les souris de laboratoire avec un type de maladie similaire \u00e0 la dystrophie musculaire de Duchenne, selon de nouvelles recherches du Smidt Heart Institute de Cedars-Sinai.<\/p>\n<p>La dystrophie musculaire de Duchenne est un trouble rare et h\u00e9r\u00e9ditaire qui affecte principalement les gar\u00e7ons et fait affaiblir tellement leurs muscles qu&rsquo;ils perdent finalement la capacit\u00e9 de marcher. Leur c\u0153ur et leurs muscles pulmonaires s&rsquo;affaiblissent \u00e9galement avec le temps, provoquant la mort pr\u00e9coce.<\/p>\n<p>La th\u00e9rapie, d\u00e9crite dans <i>Rapports de cellules souches<\/i>utilise des cellules d\u00e9riv\u00e9es de la cardiosph\u00e8re (CDC), qui sont des cellules cardiaques susceptibles de r\u00e9parer les tissus. Eduardo Marb\u00e1n, MD, Ph.D., directeur ex\u00e9cutif du Smidt Heart Institute et co-auteur de l&rsquo;\u00e9tude, a d\u00e9couvert comment isoler et d\u00e9velopper des CDC dans un laboratoire et les infuser \u00e0 un patient.<\/p>\n<p>Une \u00e9tude clinique a d\u00e9montr\u00e9 que les CDC peuvent prot\u00e9ger les muscles affaiblis de s&rsquo;affaiblir chez les adultes atteints de dystrophie musculaire de Duchenne. Des essais cliniques ont \u00e9galement montr\u00e9 que les CDC peuvent r\u00e9parer les l\u00e9sions cardiaques associ\u00e9es \u00e0 Duchenne. Une th\u00e9rapie cellulaire appel\u00e9e Deramiocel, bas\u00e9e sur les CDC, est maintenant en tests cliniques avanc\u00e9s avec des doses r\u00e9p\u00e9t\u00e9es pour v\u00e9rifier l&rsquo;am\u00e9lioration de l&rsquo;insuffisance cardiaque et de la myopathie squelettique chez les patients atteints de Duchenne.<\/p>\n<p>\u00ab\u00a0Nos nouvelles recherches d\u00e9montrent que si nous exposons de jeunes souris avec ce trouble aux CDC, nous pouvons emp\u00eacher le d\u00e9veloppement de la faiblesse musculaire de se d\u00e9velopper\u00a0\u00bb, a d\u00e9clar\u00e9 Russell G. Rogers, Ph.D., professeur adjoint au Smidt Heart Institute et auteur correspondant de l&rsquo;\u00e9tude.<\/p>\n<p>Les enqu\u00eateurs ont administr\u00e9 la th\u00e9rapie cellulaire mensuellement \u00e0 des souris de laboratoire avec une dystrophie musculaire de Duchenne au cours d&rsquo;une ann\u00e9e. Au bout d&rsquo;un an, les souris qui ont re\u00e7u la th\u00e9rapie cellulaire ont conserv\u00e9 l&rsquo;endurance et la force musculaire, ce qui \u00e9tait similaire au moment o\u00f9 les souris \u00e9taient jeunes. Cependant, les souris qui n&rsquo;ont pas re\u00e7u la th\u00e9rapie cellulaire ont perdu la capacit\u00e9 de faire de l&rsquo;exercice et leurs muscles sont devenus plus faibles, comme cela se produit pendant la progression naturelle de la dystrophie musculaire de Duchenne.<\/p>\n<p>                                        <!-- print only --><\/p><\/div>\n","protected":false},"excerpt":{"rendered":"<p>Une th\u00e9rapie cellulaire pr\u00e9serve la structure musculaire et la fonction chez les souris de laboratoire<\/p>\n","protected":false},"author":1,"featured_media":8401,"comment_status":"closed","ping_status":"","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[86],"tags":[386,44,2491,2902,2900,3823,49,1047,2901,1266,1063],"class_list":["post-8400","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-les-maladies","tag-cellulaire","tag-dans","tag-dommages","tag-duchenne","tag-dystrophie","tag-empeche","tag-les","tag-modele","tag-musculaire","tag-souris","tag-therapie","generate-columns","tablet-grid-50","mobile-grid-100","grid-parent","grid-50","resize-featured-image"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v23.4 - 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