{"id":8072,"date":"2025-07-21T02:56:56","date_gmt":"2025-07-21T00:56:56","guid":{"rendered":"https:\/\/rvh-synergie.org\/actualites\/une-strategie-therapeutique-potentielle-pourrait-aider-a-prevenir-les-complications-de-la-drepanocytose\/"},"modified":"2025-07-21T02:56:57","modified_gmt":"2025-07-21T00:56:57","slug":"une-strategie-therapeutique-potentielle-pourrait-aider-a-prevenir-les-complications-de-la-drepanocytose","status":"publish","type":"post","link":"https:\/\/rvh-synergie.org\/actualites\/une-strategie-therapeutique-potentielle-pourrait-aider-a-prevenir-les-complications-de-la-drepanocytose\/","title":{"rendered":"Une strat\u00e9gie th\u00e9rapeutique potentielle pourrait aider \u00e0 pr\u00e9venir les complications de la dr\u00e9panocytose"},"content":{"rendered":"<div>\n<div class=\"article-gallery lightGallery\">\n<div data-thumb=\"https:\/\/scx1.b-cdn.net\/csz\/news\/tmb\/2025\/study-identifies-poten-4.jpg\" data-src=\"https:\/\/scx2.b-cdn.net\/gfx\/news\/2025\/study-identifies-poten-4.jpg\" data-sub-html=\"Complement pathway schema and hemoglobin (Hb) concentrations in patients during acute chest syndrome (ACS) and at baseline. (A) Schema of complement pathway with highlighted activation proteins analyzed in this study. (B) Hb concentrations from 27 patients during ACS (Acute) and 4 to 8 weeks after hospitalization (Baseline). Data are presented as a box and whisker plot showing minimum to maximum values and all data points. Statistical analysis was performed using a paired two-tailed t-test. ****p &lt; 0.0001. Credit: &lt;i&gt;Science Translational Medicine&lt;\/i&gt; (2025). DOI: 10.1126\/scitranslmed.adl4922\">\n<figure class=\"article-img\">\n<\/figure><\/div>\n<\/div>\n<p>La dr\u00e9panocytose peut entra\u00eener une complication grave connue sous le nom de syndrome thoracique aigu\u00eb (ACS), mais les m\u00e9canismes sous-jacents ne sont pas bien compris.<\/p>\n<p>Une nouvelle \u00e9tude men\u00e9e par les chercheurs du g\u00e9n\u00e9ral de masse Brigham a identifi\u00e9 une ancienne voie immunitaire qui est activ\u00e9e chez les patients atteints de SCA et sert de moteur cl\u00e9 de la maladie. Le blocage de cette voie avec des m\u00e9dicaments cliniquement approuv\u00e9s a att\u00e9nu\u00e9 la gravit\u00e9 de la maladie dans les mod\u00e8les pr\u00e9cliniques. Les r\u00e9sultats sont publi\u00e9s dans <i>M\u00e9decine translationnelle scientifique<\/i>.<\/p>\n<p>\u00ab\u00a0Bien que l&rsquo;ACS soit la principale cause de mortalit\u00e9 chez les patients atteints de dr\u00e9panocytose, nous ne pouvons actuellement offrir des soins de soutien \u00e0 nos patients\u00a0\u00bb, a d\u00e9clar\u00e9 l&rsquo;auteur correspondant Sean Stowell, MD, Ph.D., du D\u00e9partement de pathologie du Brigham and Women&rsquo;s Hospital. \u00ab\u00a0Notre \u00e9tude offre des cibles potentielles pour une intervention th\u00e9rapeutique pour cette condition d\u00e9vastatrice.\u00a0\u00bb<\/p>\n<p>La dr\u00e9panocytose survient en raison d&rsquo;une mutation h\u00e9r\u00e9ditaire de l&rsquo;h\u00e9moglobine qui provoque la destruction des globules rouges (globules rouges) ou de l&rsquo;h\u00e9molyse. Ceci, \u00e0 son tour, peut bloquer les vaisseaux sanguins, blesser les poumons et finalement progresser en AC &#8211; une condition qui comprend un essoufflement, des douleurs thoraciques et une respiration sifflante qui peuvent rapidement progresser et devenir mortelles.<\/p>\n<p>Des recherches ant\u00e9rieures ont sugg\u00e9r\u00e9 que l&rsquo;h\u00e9molyse peut activer le syst\u00e8me de compl\u00e9ment &#8211; un groupe de prot\u00e9ines immunitaires qui d\u00e9clenchent une cascade d&rsquo;\u00e9v\u00e9nements pour \u00e9liminer les agents pathog\u00e8nes. Cependant, on ne sait pas comment le syst\u00e8me de compl\u00e9ment contribue \u00e0 l&rsquo;ACS et \u00e0 la progression de la maladie.<\/p>\n<p>L&rsquo;\u00e9quipe de recherche a analys\u00e9 les \u00e9chantillons de sang de 27 patients atteints de dr\u00e9panocytose et a d\u00e9tect\u00e9 des niveaux de base plus \u00e9lev\u00e9s d&rsquo;activation du compl\u00e9ment par rapport aux t\u00e9moins sains. Ils ont \u00e9galement observ\u00e9 une activation accrue du compl\u00e9ment chez les patients souffrant de SCA. En utilisant un mod\u00e8le de souris de dr\u00e9panocytose, les chercheurs ont constat\u00e9 que la voie du compl\u00e9ment a contribu\u00e9 \u00e0 provoquer la d\u00e9gradation des globules rouges, ce qui indique que des facteurs autres que les globules rouges mut\u00e9s peuvent contribuer aux sympt\u00f4mes de la dr\u00e9panocytose.<\/p>\n<p>Ils ont \u00e9galement constat\u00e9 que la d\u00e9gradation des globules rouges caus\u00e9e par l&rsquo;activation du compl\u00e9ment avait cr\u00e9\u00e9 un cycle de plus d&rsquo;activation, ce qui a conduit \u00e0 ACS. En \u00e9liminant certaines prot\u00e9ines de compl\u00e9ment ou en utilisant des m\u00e9dicaments existants pour les bloquer, les chercheurs ont pu r\u00e9duire la d\u00e9gradation des globules rouges et pr\u00e9venir le SCA dans leurs \u00e9tudes avec des mod\u00e8les animaux.<\/p>\n<p>Les auteurs proposent que des essais cliniques randomis\u00e9s pourraient \u00eatre men\u00e9s pour voir si des inhibiteurs du compl\u00e9ment qui ciblent diff\u00e9rentes parties de la voie pourraient \u00eatre efficaces chez les patients atteints de SCA.<\/p>\n<p>                                        <!-- print only --><\/p><\/div>\n","protected":false},"excerpt":{"rendered":"<p>La dr\u00e9panocytose peut entra\u00eener une complication grave connue sous le nom de syndrome thoracique aigu\u00eb<\/p>\n","protected":false},"author":1,"featured_media":8073,"comment_status":"closed","ping_status":"","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[86],"tags":[264,1560,881,49,651,203,538,650,768,47],"class_list":["post-8072","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-les-maladies","tag-aider","tag-complications","tag-drepanocytose","tag-les","tag-potentielle","tag-pourrait","tag-prevenir","tag-strategie","tag-therapeutique","tag-une","generate-columns","tablet-grid-50","mobile-grid-100","grid-parent","grid-50","resize-featured-image"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v23.4 - 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